Stem Cell Gene Therapy for Sickle Cell Disease

Published 2023-09-04

In new research published in the New England Journal of Medicine, scientists from multiple acacemic children's hospitals including the University of Chicago took part in the a clinical trial using the CRISPR gene editing tool to disrupt the HBG1 and HBG2 (γ-globin) gene promoters. This lead to an increase in fetal hemoglobin expression in Red Blood Cells. Clinical trial participants experienced a significant decrease in vaso-occlusive events.

Search our Directory

AABRM Members are not only experts in regenerative medicine but offer a wide range of related products, services and related-procedures in that field. Search our extensive Member Directory to find a Member near you.

Member Directory

American Society of Regenerative Medicine Logo

Excellence.  Education.  Research.  Practice.